Ultragenyx’s Dojolvi Gets FDA Nod to Treat Rare Disease

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Image: Bigstock Ultragenyx Pharmaceutical Inc. ( RARE – Free Report ) announced that the FDA has approved UX007 (triheptanoin) as a source of calories and fatty acids for the treatment of pediatric and adult patients with molecularly confirmed long-chain fatty acid oxidation disorders (LC-FAOD). The drug will be marketed […]