Published April 16, 2026
April 16, 2026 NOTES TO EDITORSAbout KhondrionKhondrion is a late-stage clinical biopharmaceutical company focused on developing therapies forpatients with primary mitochondrialRelated to the mitochondria. disease (PMD). Its lead asset, sonlicromanol, is a brain-penetrantredox […]
Published April 9, 2026
March 31, 2026 Dear Members of the PDCD Community, We are deeply grateful for your support and advocacy throughout this process, particularly aswe have worked to navigate the FDA’s Complete […]
Published November 5, 2025
FOR IMMEDIATE RELEASE Contact:Emily GrandahlMarketing Coordinator, MitoActionemily@mitoaction.org(888) 648-6228www.mitoaction.org FDA Approval of KYGEVVI Marks a Defining Moment for Mitochondrial Disease Community and Families Affected by TK2d Boston, MA — November 3, […]
Published November 3, 2025
Originally Published by Tisento Therapeutics on November 3, 2025. Findings Demonstrate the Importance of Addressing Both FatigueThe overall feeling of tiredness or lack of energy. It is not the same as simply feeling drowsy or sleepy. Being fatigued means having no motivation or energy. and Cognitive Symptoms of MELAS CAMBRIDGE, Mass., November 3, 2025 – Tisento Therapeutics […]
Published September 24, 2025
“The approval of FORZINITY, the first treatment option for Barth syndromeA rare, genetic disorder of lipid metabolism that primarily affects males. and the first approved mitochondria-targeted therapeutic, is a pivotal victory for the Barth syndrome community and offers hope for […]
Published September 24, 2025
Company honored in its commitment to patients and families living with mitochondrial disease; invites the community to walk with BPGbio colleagues and MitoAction BOSTON, MA — September 12, 2025 — BPGbio, […]
Published September 4, 2025
Earlier today, Saol Therapeutics shared the U.S. Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL) regarding the company’s application for dichloroacetateInvestigational drug for treatment of mitochondrial disease. A small inorganic molecule that increases the rate of oxidative phosphorylation, the main pathway by which the energy in food is converted (DCA) to treat Pyruvate Dehydrogenase Complex Deficiency […]
Published April 1, 2024
FOR IMMEDIATE RELEASE [Boston, MA, April 1, 2024] – MitoAction, a leading nonprofit organization dedicated to improving the lives of individuals and families affected by mitochondrial disease, recently convened a […]
Published February 25, 2024
The Lurie Prize in Biomedical Sciences recognizes outstanding achievement by a promising young scientist (52 or younger) in biomedical research. It is worth $100,000, and awarded annually by the Foundation […]
Published February 24, 2024
https://cob.silverchair-cdn.com/cob/content_public/journal/bio/jam/10.1242_bio.060278/3/bio060278.pdf?Expires=1711827491&Signature=G4px-hX-CQRWqXepaWcuG0-Y-QYF06N9pma-LYMFv5E9CQq~vlJaOQI2uuSjvfqBwOSWi3OMmI79SiubfEXv94SN1ek0zC2F01FEYHL7El0mIQtZ-GTaXhO6IjvA-oOCPOcMpSjZomYdtICQ2E9FpDyRKP70OsoFX-c2qxbyQ6LnPrRgiFgfraB~UqADJy-WSqYrLgNvjSfnUXahRkSo45PxA9pSq8kAm8Pxjivc59PF27oDji~p2dufwrRQlCvYKzjcgaPRg43qMsmTh8DML0rdu1BZWnxueti5C-Rr6znyJPQQfRWDoQw1JVg28p9n15vtBkZjOIRdKg04gKVFSw__&Key-Pair-Id=APKAIE5G5CRDK6RD3PGA One of the great scientific discoveries of the 20th century is the extraordinary similarity among all living species at the molecular level, despite the extreme diversity of their appearance […]
