Expert Series: Off Label, On the Table: Therapeutic Approaches to Rhabdomyolysis and Myositis in Long-Chain Fatty Acid Oxidation Disorders 

What happens when challenging complications of long-chain fatty acid oxidation disorders call for treatment approaches beyond established practice? April Lehman will share their center’s experience using steroids and biologics in the management of rhabdomyolysis and myositis in LC-FAOD, highlighting their clinical rationale, observations, and unanswered questions. These experiences underscore the need for collaborative studies to better define the role, safety, and efficacy of these therapies to give our patients the best possible outcomes.