Barth Syndrome – When the Lack of Fair, Equitable and Appropriate Regulatory Review Process Jeopardizes Ultra-Rare Drug Development Barth Syndrome Foundation Executive Director Emily Milligan, and Director of Family Services […]
Rhabdomyolysis can feel like being lost without a road map leading you home. Join us for an informal session to discuss personal experiences with rhabdo, from symptoms to recovery. Physical […]
Dr. Jerry Vockley provides updates on the latest in therapy development for the FAOD community at the 2022 International Metabolic Conference.
Join MitoAction and Dr. Jan Smeitink, CEO of Khondrion for our our March Expert Series presentation. MELAS spectrum (m.3243A>G) disorders belong to the most frequently encountered group of primary mitochondrial […]
Join MitoAction and Acton Pharmacy’s Clinical Pharmacist, Ted Toufas as we revisit and provide the latest updates about the mito cocktail! The mito cocktail is one of the front-line treatment […]