Current Clinical Trials

To view a complete listing of all clinical trials related to mitochondrial disease, please visit clincialtrials.gov.

Click each box below to view the details of these featured clinical trials.

Phase 2a Study of IW-6463 in Adults Diagnosed With MELAS

The KHENERGYZE Study (MELAS)

Efficacy and Safety of MT1621 in Thymidine Kinase 2 (TK2) Deficiency

Efficacy and Safety of 24 Week Treatment With REN001 in Patients With Primary Mitochondrial Myopathy

Prospective Study of the Disease Characteristics of Adult Patients With LC Fatty Acid Oxidation Disorders

PTC743 - MIT-E

Aromatic L-amino Acid Decarboxylase (AADC)

Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency: (DCA/PDCD)

LC-FAOD Odyssey Study